Skip to main page content
U.S. flag

An official website of the United States government

Dot gov

The .gov means it’s official.
Federal government websites often end in .gov or .mil. Before sharing sensitive information, make sure you’re on a federal government site.

Https

The site is secure.
The https:// ensures that you are connecting to the official website and that any information you provide is encrypted and transmitted securely.

Access keys NCBI Homepage MyNCBI Homepage Main Content Main Navigation

Search Page

Filters

My NCBI Filters

Results by year

Table representation of search results timeline featuring number of search results per year.

Year Number of Results
2009 1
2010 2
2011 1
2015 1
2016 2
2017 2
2018 3
2019 8
2020 12
2021 10
2022 8
2023 7
2024 0

Text availability

Article attribute

Article type

Publication date

Search Results

46 results

Results by year

Filters applied: . Clear all
Page 1
Initial results from a first-in-human gene therapy trial on X-linked retinitis pigmentosa caused by mutations in RPGR.
Cehajic-Kapetanovic J, Xue K, Martinez-Fernandez de la Camara C, Nanda A, Davies A, Wood LJ, Salvetti AP, Fischer MD, Aylward JW, Barnard AR, Jolly JK, Luo E, Lujan BJ, Ong T, Girach A, Black GCM, Gregori NZ, Davis JL, Rosa PR, Lotery AJ, Lam BL, Stanga PE, MacLaren RE. Cehajic-Kapetanovic J, et al. Nat Med. 2020 Mar;26(3):354-359. doi: 10.1038/s41591-020-0763-1. Epub 2020 Feb 24. Nat Med. 2020. PMID: 32094925 Free PMC article. Clinical Trial.
Bioengineering strategies for restoring vision.
Cehajic-Kapetanovic J, Singh MS, Zrenner E, MacLaren RE. Cehajic-Kapetanovic J, et al. Nat Biomed Eng. 2023 Apr;7(4):387-404. doi: 10.1038/s41551-021-00836-4. Epub 2022 Jan 31. Nat Biomed Eng. 2023. PMID: 35102278 Review.
Molecular Therapies for Choroideremia.
Cehajic Kapetanovic J, Barnard AR, MacLaren RE. Cehajic Kapetanovic J, et al. Genes (Basel). 2019 Sep 23;10(10):738. doi: 10.3390/genes10100738. Genes (Basel). 2019. PMID: 31548516 Free PMC article. Review.
Molecular Strategies for RPGR Gene Therapy.
Cehajic Kapetanovic J, McClements ME, Martinez-Fernandez de la Camara C, MacLaren RE. Cehajic Kapetanovic J, et al. Genes (Basel). 2019 Sep 4;10(9):674. doi: 10.3390/genes10090674. Genes (Basel). 2019. PMID: 31487940 Free PMC article. Review.
Gene-agnostic therapeutic approaches for inherited retinal degenerations.
John MC, Quinn J, Hu ML, Cehajic-Kapetanovic J, Xue K. John MC, et al. Among authors: cehajic kapetanovic j. Front Mol Neurosci. 2023 Jan 9;15:1068185. doi: 10.3389/fnmol.2022.1068185. eCollection 2022. Front Mol Neurosci. 2023. PMID: 36710928 Free PMC article. Review.
Genome-Editing Strategies for Treating Human Retinal Degenerations.
Quinn J, Musa A, Kantor A, McClements ME, Cehajic-Kapetanovic J, MacLaren RE, Xue K. Quinn J, et al. Among authors: cehajic kapetanovic j. Hum Gene Ther. 2021 Mar;32(5-6):247-259. doi: 10.1089/hum.2020.231. Epub 2020 Nov 19. Hum Gene Ther. 2021. PMID: 32993386 Free PMC article. Review.
RPGR gene therapy presents challenges in cloning the coding sequence.
Martinez-Fernandez De La Camara C, Cehajic-Kapetanovic J, MacLaren RE. Martinez-Fernandez De La Camara C, et al. Among authors: cehajic kapetanovic j. Expert Opin Biol Ther. 2020 Jan;20(1):63-71. doi: 10.1080/14712598.2020.1680635. Epub 2019 Oct 20. Expert Opin Biol Ther. 2020. PMID: 31612744 Free PMC article. Review.
CRISPR genome engineering for retinal diseases.
Kantor A, McClements ME, Peddle CF, Fry LE, Salman A, Cehajic-Kapetanovic J, Xue K, MacLaren RE. Kantor A, et al. Among authors: cehajic kapetanovic j. Prog Mol Biol Transl Sci. 2021;182:29-79. doi: 10.1016/bs.pmbts.2021.01.024. Epub 2021 Mar 19. Prog Mol Biol Transl Sci. 2021. PMID: 34175046
46 results