Three-year results of phase I retinal gene therapy trial for CNGA3-mutated achromatopsia: results of a non randomised controlled trial
Felix Friedrich Reichel, Stylianos Michalakis, Barbara Wilhelm, Ditta Zobor, Regine Muehlfriedel, Susanne Kohl, Nicole Weisschuh, Vithiyanjali Sothilingam, Laura Kuehlewein, Nadine Kahle, Immanuel Seitz, Francois Paquet-Durand, Stephen H Tsang, Peter Martus, Tobias Peters, Mathias Seeliger, Karl Ulrich Bartz-Schmidt, Marius Ueffing, Eberhard Zrenner, Martin Biel, Bernd Wissinger, Dominik Fischer
British Journal of Ophthalmology Nov 2022, 106 (11) 1567-1572; DOI: 10.1136/bjophthalmol-2021-319067